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Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A
Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A
5
(693)
· $ 11.00 · In stock
Product Description
FDA Approves First Gene Therapy for Severe Hemophilia A - Southern Iowa Mental Health Center
BioMarin (BMRN) Gets FDA Nod for Hemophilia A Gene Therapy
Hemostatic Response is Maintained for up to 5 Years Following Treatment with Valoctocogene Roxaparvovec, an AAV5-hFVIII-SQ Gene Therapy for Severe Hemophilia A - ISTH Congress Abstracts
Gene therapy for hemophilia: a review on clinical benefit, limitations, and remaining issues - ScienceDirect
BioMarin Provides Additional Data from Recent 4 Year Update of Ongoing Phase 1/2 Study of Valoctocogene Roxaparvovec Gene Therapy for Severe Hemophilia A in Late-Breaking Oral Presentation at World Federation of Hemophilia
IJMS, Free Full-Text
FDA approves valoctocogene roxaparvovec gene therapy for adults with severe hemophilia A
A Molecular Revolution in the Treatment of Hemophilia - ScienceDirect
BioMarin Begins Mid Stage Study on Gene Therapy Candidate
Early Phase Clinical Immunogenicity of Valoctocogene Roxaparvovec, an AAV5-Mediated Gene Therapy for Hemophilia A: Molecular Therapy
Benefits of Valoctocogene Roxaparvovec Persist in Hemophilia A - Consumer Health News
Matching‐adjusted indirect comparison of bleeding outcomes in severe haemophilia A: Comparing valoctocogene roxaparvovec gene therapy, emicizumab prophylaxis, and FVIII replacement prophylaxis - Astermark - 2023 - Haemophilia - Wiley Online Library
Valoctocogene Roxaparvovec for Severe Hemophilia A, Pipeline